Phase I/II Trial of Liver-derived Mesenchymal Stem Cells in Pediatric Liver-based Metabolic Disorders: A Prospective, Open Label, Multicenter, Partially Randomized, Safety Study of One Cycle of Heterologous Human Adult Liver-derived Progenitor Cells (HepaStem) in Urea Cycle Disorders and Crigler-Najjar Syndrome Patients.
Stephanie Grunewald, Pierre Broué, Emmanuel Jacquemin, Ana Isabel Lopes, Isabel Gonçalves, Hanna Mandel, Joanna Pawlowska, Diana Kamińska, Eyal Shteyer, Giuliano Torre, Riki Shapiro, François Eyskens, Philippe Clapuyt, Paul Gissen, Danièle Pariente, Carlo Dionisi-Vici, Marc Yudkoff, Maria Mercedes Binda, Mustapha Najimi, Nathalie Belmonte, Beatrice de Vos, Joelle Thonnard, Etienne Sokal, Patrick McKiernan, Dries Dobbelaere, Françoise Smets
Transplantation 2020;103(9):1903-1915