Effect of Poloxamer 188 vs Placebo on Painful Vaso-Occlusive Episodes in Children and Adults With Sickle Cell Disease: A Randomized Clinical Trial.
James F Casella, Bruce A Barton, Julie Kanter, L Vandy Black, Suvankar Majumdar, Adlette Inati, Yasser Wali, Richard A Drachtman, Miguel R Abboud, Yurdanur Kilinc, Beng R Fuh, Murtadha K Al-Khabori, Clifford M Takemoto, Emad Salman, Sharada A Sarnaik, Nirmish Shah, Claudia R Morris, Jennifer Keates-Baleeiro, Ashok Raj, Ofelia A Alvarez, Lewis L Hsu, Alexis A Thompson, India Y Sisler, Betty S Pace, Suzie A Noronha, Joseph L Lasky, Elena Cela de Julian, Kamar Godder, Courtney Dawn Thornburg, Natalie L Kamberos, Rachelle Nuss, Anne M Marsh, William C Owen, Anne Schaefer, Cameron K Tebbi, Christophe F Chantrain, Debra E Cohen, Zeynep Karakas, Connie M Piccone, Alex George, Jason M Fixler, Tammuella C Singleton, Thomas Moulton, Charles T Quinn, Clarisse Lopes de Castro Lobo, Abdulkareem M Almomen, Meenakshi Goyal-Khemka, Philip Maes, Marty Emanuele, Rebecca T Gorney, Claire S Padgett, Ed Parsley, Shari S Kronsberg, Gregory J Kato, Mark T Gladwin
JAMA 2021;325(15):1513-1523