Efficacy and safety clinical trial with efavirenz in patients diagnosed with adult Niemann-pick type C with cognitive impairment.
Imma Rico, María Cerdán Sánchez, Celia Pérez-Sousa, Laura Rodríguez-Bel, Montserrat Cortés-Romera, Eugenia de Lama, Mònica Cos, Nahum Calvo-Malvar, Jaume Campdelacreu-Fumadó, Cristina Sánchez-Castañeda, Nuria Muelas, María Dolores Ledesma, Thiago Carnaval, Roser Llop, Petru Cristian Simon, Jordi Gascón-Bayarri, Sebastián Videla, Anna Ferrer, Adolfo López de Munain, Pablo Mir, María Dolores Sevillano
Medicine 2022;101(48):e31471