Clinical trial of L-Carnitine and valproic acid in spinal muscular atrophy type I.
Kristin J Krosschell, John T Kissel, Elise L Townsend, Sarah D Simeone, Ren Zhe Zhang, Sandra P Reyna, Thomas O Crawford, Mary K Schroth, Gyula Acsadi, Priya S Kishnani, Jürgen-Christoph Von Kleist-Retzow, Barbara Hero, Guy D'Anjou, Edward C Smith, Bakri Elsheikh, Louise R Simard, Thomas W Prior, Charles B Scott, Bernard Lasalle, Ai Sakonju, Brunhilde Wirth, Kathryn J Swoboda
Muscle & nerve 2019;57(2):193-199