Impact of interventional and non-interventional variables on anthropometric long-term development in glutaric aciduria type 1: A national prospective multi-centre study.
E M Charlotte Märtner, Esther M Maier, Katharina Mengler, Eva Thimm, Katharina A Schiergens, Thorsten Marquardt, René Santer, Natalie Weinhold, Iris Marquardt, Anibh M Das, Peter Freisinger, Sarah C Grünert, Judith Vossbeck, Robert Steinfeld, Matthias R Baumgartner, Skadi Beblo, Andrea Dieckmann, Andrea Näke, Martin Lindner, Jana Heringer-Seifert, Dominic Lenz, Georg F Hoffmann, Chris Mühlhausen, Regina Ensenauer, Sven F Garbade, Stefan Kölker, Nikolas Boy
Journal of inherited metabolic disease 2021;44(3):629-638