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Results for
""Compassionate Use Trials""[mesh_terms]

21 Results

Searching titles within these results

Long-term add-on therapy (compassionate use) with oral artesunate in patients with metastatic breast cancer after participating in a phase I study (ARTIC M33/2).

Cornelia von Hagens, Ingeborg Walter-Sack, Maren Goeckenjan, Brigitte Storch-Hagenlocher, Serkan Sertel, Michael Elsässer, Bjoern A Remppis, Judith Munzinger, Lutz Edler, Thomas Efferth, Andreas Schneeweiss, Thomas Strowitzki

Phytomedicine : international journal of phytotherapy and phytopharmacology 2019;54():140-148

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Expanded Access Programs, compassionate drug use, and Emergency Use Authorizations during the COVID-19 pandemic.

Youssef Rizk, Mandeep R Mehra, John G Rizk, Donald N Forthal, Kamyar Kalantar-Zadeh, Carl J Lavie, JoAnn P Pfeiffer, John C Lewin

Drug discovery today 2021;26(2):593-603

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Efficacy and safety of cyclic pyranopterin monophosphate substitution in severe molybdenum cofactor deficiency type A: a prospective cohort study.

Bernd C Schwahn, Francjan J Van Spronsen, Abdel A Belaidi, Stephen Bowhay, John Christodoulou, Terry G Derks, Julia B Hennermann, Elisabeth Jameson, Kai König, Tracy L McGregor, Esperanza Font-Montgomery, José A Santamaria-Araujo, Saikat Santra, Mamta Vaidya, Anne Vierzig, Evangeline Wassmer, Ilona Weis, Flora Y Wong, Alex Veldman, Günter Schwarz

Lancet (London, England) 2016;386(10007):1955-1963

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Balloon expandable transcatheter heart valves for native mitral valve disease with severe mitral annular calcification.

Mayra Guerrero, Marina Urena, Amit Pursnani, Dee D Wang, Alec Vahanian, William O'Neill, Ted Feldman, Dominique Himbert

The Journal of cardiovascular surgery 2016;57(3):401-9

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Pharmacogenetic Predictors of Cannabidiol Response and Tolerability in Treatment-Resistant Epilepsy.

Brittney H Davis, T Mark Beasley, Michelle Amaral, Jerzy P Szaflarski, Tyler Gaston, Leslie Perry Grayson, David G Standaert, E Martina Bebin, Nita A Limdi

Clinical pharmacology and therapeutics 2021;110(5):1368-1380

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Changes in stress, eating, and metabolic factors are related to changes in telomerase activity in a randomized mindfulness intervention pilot study.

Jennifer Daubenmier, Jue Lin, Elizabeth Blackburn, Frederick M Hecht, Jean Kristeller, Nicole Maninger, Margaret Kuwata, Peter Bacchetti, Peter J Havel, Elissa Epel

Psychoneuroendocrinology 2012;37(7):917-28

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EPI-743 reverses the progression of the pediatric mitochondrial disease--genetically defined Leigh Syndrome.

Diego Martinelli, Michela Catteruccia, Fiorella Piemonte, Anna Pastore, Giulia Tozzi, Carlo Dionisi-Vici, Giuseppe Pontrelli, Tiziana Corsetti, Susanna Livadiotti, Viktoria Kheifets, Andrew Hinman, William D Shrader, Martin Thoolen, Matthew B Klein, Enrico Bertini, Guy Miller

Molecular genetics and metabolism 2013;107(3):383-8

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Expert opinion on mexiletine treatment in adult patients with myotonic dystrophy.

Josselin Duchateau, Guillaume Bassez, Fabien Labombarda, Jean-Marc Sellal, Karim Wahbi, Jean-Claude Deharo, Jean-François Desaphy, Savine Vicart, Emmanuelle Salort-Campana

Archives of cardiovascular diseases 2024;117(6-7):450-456

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Efficacy and safety of cinacalcet for the treatment of secondary hyperparathyroidism in patients with advanced chronic kidney disease before initiation of regular dialysis.

Jesús Montenegro, Iñaki Cornago, Isabel Gallardo, Paula García-Ledesma, Ainhoa Hernando, Isabel Martinez, Rosa I Muñoz, Marco A Romero

Nephrology (Carlton, Vic.) 2012;17(1):26-31

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New therapeutic approach in Dravet syndrome and Lennox-Gastaut syndrome with cannabidiol.

V Villanueva, M Carreño-Martínez, A Gil Nagel-Rein, F J López-González

Revista de neurologia 2022;72(S01):S1-S10

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Final results of the European Advanced Renal Cell Carcinoma Sorafenib (EU-ARCCS) expanded-access study: a large open-label study in diverse community settings.

J Beck, G Procopio, E Bajetta, U Keilholz, S Negrier, C Szczylik, C Bokemeyer, S Bracarda, D J Richel, M Staehler, U P Strauss, S Mersmann, K Burock, B Escudier

Annals of oncology : official journal of the European Society for Medical Oncology 2011;22(8):1812-23

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Rebound effect after intravitreal dexamethasone implant for the treatment of macular edema secondary to central retinal vein occlusion.

Maurizio Battaglia Parodi, Pierluigi Iacono, Umberto De Benedetto, Marialucia Cascavilla, Francesco Bandello

Journal of ocular pharmacology and therapeutics : the official journal of the Association for Ocular Pharmacology and Therapeutics 2013;28(6):566-8

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Response to sorafenib treatment in advanced metastatic thyroid cancer.

Fabian Pitoia

Arquivos brasileiros de endocrinologia e metabologia 2015;58(1):37-41

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Effectivenesss of ivacaftor in severe cystic fibrosis patients and non-G551D gating mutations.

Donatello Salvatore, Vincenzo Carnovale, Paola Iacotucci, Cesare Braggion, Carlo Castellani, Giuseppe Cimino, Carmela Colangelo, Michela Francalanci, Giuseppina Leonetti, Vincenzina Lucidi, Antonio Manca, Pamela Vitullo, Nicola Ferrara

Pediatric pulmonology 2020;54(9):1398-1403

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Potential therapy of multidrug-resistant and extremely drug-resistant tuberculosis with thioridazine.

Leonard Amaral, Joseph Molnar

In vivo (Athens, Greece) 2012;26(2):231-6

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Results: 1 – 15 / 21

Filters

Expert Opinion

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Results for ""Compassionate Use Trials""[mesh_terms]

Long-term add-on therapy (compassionate use) with oral artesunate in patients with metastatic breast cancer after participating in a phase I study (ARTIC M33/2).

Expanded Access Programs, compassionate drug use, and Emergency Use Authorizations during the COVID-19 pandemic.

Efficacy and safety of cyclic pyranopterin monophosphate substitution in severe molybdenum cofactor deficiency type A: a prospective cohort study.

Balloon expandable transcatheter heart valves for native mitral valve disease with severe mitral annular calcification.

Pharmacogenetic Predictors of Cannabidiol Response and Tolerability in Treatment-Resistant Epilepsy.

Changes in stress, eating, and metabolic factors are related to changes in telomerase activity in a randomized mindfulness intervention pilot study.

EPI-743 reverses the progression of the pediatric mitochondrial disease--genetically defined Leigh Syndrome.

Expert opinion on mexiletine treatment in adult patients with myotonic dystrophy.

Efficacy and safety of cinacalcet for the treatment of secondary hyperparathyroidism in patients with advanced chronic kidney disease before initiation of regular dialysis.

New therapeutic approach in Dravet syndrome and Lennox-Gastaut syndrome with cannabidiol.

Final results of the European Advanced Renal Cell Carcinoma Sorafenib (EU-ARCCS) expanded-access study: a large open-label study in diverse community settings.

Rebound effect after intravitreal dexamethasone implant for the treatment of macular edema secondary to central retinal vein occlusion.

Response to sorafenib treatment in advanced metastatic thyroid cancer.

Effectivenesss of ivacaftor in severe cystic fibrosis patients and non-G551D gating mutations.

Potential therapy of multidrug-resistant and extremely drug-resistant tuberculosis with thioridazine.

Results for
""Compassionate Use Trials""[mesh_terms]